CYCLOPHOSPHAMIDE

85/100 · Critical

Manufactured by Avyxa Pharma, LLC

High Safety Concerns with Cyclophosphamide Use

284,202 FDA adverse event reports analyzed

Last updated: 2026-05-12

About CYCLOPHOSPHAMIDE

CYCLOPHOSPHAMIDE is a medication tracked in the FDA Adverse Event Reporting System (FAERS), manufactured by Avyxa Pharma, LLC. Based on analysis of 284,202 FDA adverse event reports, CYCLOPHOSPHAMIDE has a safety score of 85 out of 100. This score indicates a relatively favorable safety profile, with fewer or less severe adverse events compared to many other tracked medications. The most commonly reported adverse reactions for CYCLOPHOSPHAMIDE include OFF LABEL USE, FEBRILE NEUTROPENIA, NEUTROPENIA, DRUG INEFFECTIVE, PYREXIA. This page provides a comprehensive breakdown of reported side effects, safety signals, patient demographics, and AI-powered safety analysis for CYCLOPHOSPHAMIDE.

AI Safety Analysis

Cyclophosphamide has a safety concern score of 85 out of 100, placing it in the high concern category based on analysis of FDA adverse event data. The FDA has received approximately 284,202 adverse event reports for this medication, which is primarily manufactured by Avyxa Pharma, Llc.

The most commonly reported adverse events include Off Label Use, Febrile Neutropenia, Neutropenia. Of classified reports, 96.2% were designated as serious by the FDA, meaning they involved hospitalization, disability, or other significant medical outcomes. Cyclophosphamide is associated with a high incidence of serious adverse reactions, including infections and hematological toxicity.

The drug is frequently reported to cause severe neutropenia and thrombocytopenia, indicating significant risk of life-threatening complications. There is a notable risk of disease progression and recurrence, suggesting the drug may not always achieve long-term remission.

Patients taking Cyclophosphamide should monitor for the commonly reported side effects and contact their healthcare provider if they experience any unusual symptoms. Cyclophosphamide can interact with other drugs, particularly those affecting bone marrow function, leading to increased toxicity. Warnings include monitoring for interactions and adjusting dosages accordingly. This analysis is based on voluntary FDA adverse event reports and should not replace professional medical advice.

Safety Score: 85/100

Cyclophosphamide received a safety concern score of 85/100 (high concern). This is based on a 96.2% serious event ratio across 168,881 classified reports. The score accounts for 284,202 total adverse event reports and 100 distinct reaction types. This high score reflects a significant proportion of serious adverse events in the reporting data.

Top Adverse Reactions

OFF LABEL USE15,422 reports
FEBRILE NEUTROPENIA13,977 reports
NEUTROPENIA10,160 reports
DRUG INEFFECTIVE10,098 reports
PYREXIA8,898 reports
DISEASE PROGRESSION7,781 reports
PNEUMONIA6,373 reports
PRODUCT USE IN UNAPPROVED INDICATION6,307 reports
THROMBOCYTOPENIA6,212 reports
NAUSEA5,977 reports
ANAEMIA5,852 reports
SEPSIS5,506 reports
DIARRHOEA5,288 reports
DEATH5,066 reports
VOMITING4,702 reports
INFECTION4,446 reports
PANCYTOPENIA4,099 reports
FATIGUE4,082 reports
WHITE BLOOD CELL COUNT DECREASED4,082 reports
MYELOSUPPRESSION3,918 reports
DYSPNOEA3,688 reports
CYTOKINE RELEASE SYNDROME3,513 reports
MUCOSAL INFLAMMATION3,415 reports
NEUROPATHY PERIPHERAL3,282 reports
PLATELET COUNT DECREASED3,038 reports
ASTHENIA3,013 reports
MALIGNANT NEOPLASM PROGRESSION2,969 reports
RESPIRATORY FAILURE2,930 reports
LEUKOPENIA2,924 reports
SEPTIC SHOCK2,895 reports
NEUTROPHIL COUNT DECREASED2,883 reports
HYPOTENSION2,699 reports
ACUTE KIDNEY INJURY2,612 reports
PLASMA CELL MYELOMA2,496 reports
CONDITION AGGRAVATED2,383 reports
COVID 192,319 reports
HEADACHE2,305 reports
MYELODYSPLASTIC SYNDROME2,243 reports
CYTOMEGALOVIRUS INFECTION2,209 reports
ACUTE MYELOID LEUKAEMIA2,198 reports
ABDOMINAL PAIN2,116 reports
ALOPECIA2,071 reports
BONE MARROW FAILURE2,032 reports
COUGH2,015 reports
PAIN2,013 reports
DECREASED APPETITE2,003 reports
RENAL FAILURE1,966 reports
CARDIAC FAILURE1,944 reports
TOXICITY TO VARIOUS AGENTS1,937 reports
RASH1,934 reports
PLEURAL EFFUSION1,873 reports
HAEMOGLOBIN DECREASED1,858 reports
MULTIPLE ORGAN DYSFUNCTION SYNDROME1,773 reports
INTERSTITIAL LUNG DISEASE1,737 reports
HYPERTENSION1,704 reports
PULMONARY EMBOLISM1,694 reports
CONSTIPATION1,647 reports
STOMATITIS1,600 reports
GENERAL PHYSICAL HEALTH DETERIORATION1,591 reports
DISEASE RECURRENCE1,578 reports
DIFFUSE LARGE B CELL LYMPHOMA1,576 reports
NEOPLASM PROGRESSION1,549 reports
THERAPY PARTIAL RESPONDER1,544 reports
INTENTIONAL PRODUCT USE ISSUE1,537 reports
HAEMATOTOXICITY1,517 reports
DRUG INEFFECTIVE FOR UNAPPROVED INDICATION1,493 reports
CYTOPENIA1,474 reports
PRODUCT USE ISSUE1,464 reports
MALAISE1,456 reports
URINARY TRACT INFECTION1,409 reports
THERAPY NON RESPONDER1,396 reports
ATRIAL FIBRILLATION1,395 reports
NEUROTOXICITY1,389 reports
DIZZINESS1,380 reports
ACUTE GRAFT VERSUS HOST DISEASE1,379 reports
WEIGHT DECREASED1,361 reports
CHILLS1,349 reports
HYPOGAMMAGLOBULINAEMIA1,332 reports
ARTHRALGIA1,322 reports
ALANINE AMINOTRANSFERASE INCREASED1,321 reports
GRAFT VERSUS HOST DISEASE1,309 reports
DEHYDRATION1,264 reports
TREATMENT FAILURE1,262 reports
RENAL IMPAIRMENT1,250 reports
SECOND PRIMARY MALIGNANCY1,247 reports
VENOOCCLUSIVE LIVER DISEASE1,243 reports
LYMPHOPENIA1,229 reports
CYTOMEGALOVIRUS INFECTION REACTIVATION1,218 reports
HYPOKALAEMIA1,213 reports
DEEP VEIN THROMBOSIS1,212 reports
BACK PAIN1,203 reports
PROGRESSIVE MULTIFOCAL LEUKOENCEPHALOPATHY1,198 reports
TUMOUR LYSIS SYNDROME1,191 reports
PNEUMOCYSTIS JIROVECII PNEUMONIA1,175 reports
NEUTROPENIC SEPSIS1,172 reports
CARDIOTOXICITY1,170 reports
LYMPHADENOPATHY1,170 reports
AGRANULOCYTOSIS1,164 reports
TACHYCARDIA1,164 reports
HERPES ZOSTER1,159 reports

Key Safety Signals

  • Frequent reports of febrile neutropenia and pneumonia highlight the risk of severe infections.
  • High incidence of hematological toxicity, including anemia and leukopenia, indicates significant risk to blood cell production.
  • Multiple reports of disease progression and recurrence suggest limited efficacy in some patients.

Patient Demographics

Adverse event reports by sex: Female: 74,263, Male: 62,143, Unknown: 1,336. The most frequently reported age groups are age 60 (2,827 reports), age 65 (2,741 reports), age 62 (2,668 reports). These demographics reflect reporting patterns and may not represent the full patient population.

Report Outcomes

Out of 168,881 classified reports for CYCLOPHOSPHAMIDE:

  • Serious: 162,467 reports (96.2%) — includes hospitalization, disability, life-threatening events, or death
  • Non-Serious: 6,414 reports (3.8%)
Serious 96.2%Non-Serious 3.8%

The FDA classifies an adverse event as “serious” if it results in death, hospitalization, disability, congenital anomaly, or requires intervention to prevent permanent damage.

Demographics Breakdown

Reports by Sex

Female74,263 (53.9%)
Male62,143 (45.1%)
Unknown1,336 (1.0%)

Reports by Age

Age 602,827 reports
Age 652,741 reports
Age 622,668 reports
Age 662,666 reports
Age 642,606 reports
Age 692,498 reports
Age 592,494 reports
Age 672,477 reports
Age 702,426 reports
Age 682,389 reports
Age 582,363 reports
Age 562,354 reports
Age 632,352 reports
Age 612,304 reports
Age 572,295 reports
Age 552,241 reports
Age 522,170 reports
Age 542,122 reports
Age 532,027 reports
Age 722,018 reports

Demographics reflect voluntary FDA adverse event reporting patterns and may not represent the full patient population.

Drug Interactions & Warnings

Cyclophosphamide can interact with other drugs, particularly those affecting bone marrow function, leading to increased toxicity. Warnings include monitoring for interactions and adjusting dosages accordingly.

What You Should Know

If you are taking Cyclophosphamide, here are important things to know. The most commonly reported side effects include off label use, febrile neutropenia, neutropenia, drug ineffective, pyrexia. While many of these may be mild and temporary, you should contact your healthcare provider if any symptoms are severe or persistent. Monitor blood counts regularly to detect early signs of hematological toxicity. Be vigilant for signs of infection, such as fever or chills, and seek medical attention immediately. Discuss potential drug interactions with your healthcare provider to minimize risk. If you experience a serious adverse reaction, seek emergency medical attention immediately or call 911. You can report side effects to the FDA's MedWatch program at 1-800-FDA-1088.

Regulatory Context

The FDA closely monitors cyclophosphamide reports, and regulatory actions may be taken based on emerging safety signals. Patients should report any adverse reactions promptly.

Frequently Asked Questions

How many adverse event reports has the FDA received for Cyclophosphamide?

The FDA has received approximately 284,202 adverse event reports associated with Cyclophosphamide. These reports come from healthcare professionals, consumers, and manufacturers through the FDA Adverse Event Reporting System (FAERS). Note that the number of reports does not directly indicate the frequency of side effects, as adverse events are voluntarily reported and may be underrepresented.

What are the most commonly reported side effects of Cyclophosphamide?

The most frequently reported adverse events for Cyclophosphamide include Off Label Use, Febrile Neutropenia, Neutropenia, Drug Ineffective, Pyrexia. By volume, the top reported reactions are: Off Label Use (15,422 reports), Febrile Neutropenia (13,977 reports), Neutropenia (10,160 reports). These figures reflect FDA adverse event reports and may not represent the true incidence rate of these side effects in all patients taking Cyclophosphamide.

What percentage of Cyclophosphamide adverse event reports are serious?

Out of 168,881 classified reports, 162,467 (96.2%) were classified as serious and 6,414 as non-serious. The FDA classifies an event as "serious" if it results in death, hospitalization, disability, or other medically significant outcomes. A higher serious-event ratio warrants closer attention but does not necessarily mean the drug is unsafe.

Who reports adverse events for Cyclophosphamide (by sex)?

Adverse event reports for Cyclophosphamide break down by patient sex as follows: Female: 74,263, Male: 62,143, Unknown: 1,336. This distribution reflects reporting patterns rather than actual risk differences between groups. Reporting rates can be influenced by prescribing patterns, disease demographics, and reporting behavior.

What age groups report the most side effects for Cyclophosphamide?

The most frequently reported age groups for Cyclophosphamide adverse events are: age 60: 2,827 reports, age 65: 2,741 reports, age 62: 2,668 reports, age 66: 2,666 reports, age 64: 2,606 reports. Age-related reporting patterns can reflect both the demographics of the patient population and potential age-related susceptibility to certain side effects.

Who manufactures Cyclophosphamide?

The primary manufacturer associated with Cyclophosphamide adverse event reports is Avyxa Pharma, Llc. Multiple manufacturers may produce generic versions of this drug. The manufacturer listed reflects the most frequently reported brand in FDA adverse event data.

What other side effects have been reported for Cyclophosphamide?

Beyond the most common reactions, other reported adverse events for Cyclophosphamide include: Disease Progression, Pneumonia, Product Use In Unapproved Indication, Thrombocytopenia, Nausea. Less common side effects can still be clinically significant. Patients should report any unusual symptoms to their healthcare provider.

How do I report a side effect from Cyclophosphamide?

You can report adverse events from Cyclophosphamide to the FDA through their MedWatch program at www.fda.gov/medwatch, by calling 1-800-FDA-1088, or by completing Form FDA 3500. Healthcare professionals, consumers, and manufacturers can all submit reports. Reporting helps the FDA monitor drug safety after approval.

What is Cyclophosphamide's safety score and what does it mean?

Cyclophosphamide has a safety concern score of 85 out of 100 (high concern). This score is calculated from the ratio of serious to non-serious adverse events, the diversity of reported reactions, and the overall volume of reports relative to usage. Cyclophosphamide is associated with a high incidence of serious adverse reactions, including infections and hematological toxicity.

What are the key safety signals for Cyclophosphamide?

Key safety signals identified in Cyclophosphamide's adverse event data include: Frequent reports of febrile neutropenia and pneumonia highlight the risk of severe infections.. High incidence of hematological toxicity, including anemia and leukopenia, indicates significant risk to blood cell production.. Multiple reports of disease progression and recurrence suggest limited efficacy in some patients.. These signals are derived from patterns in FDA reports and should be discussed with a healthcare provider for personalized assessment.

Does Cyclophosphamide interact with other drugs?

Cyclophosphamide can interact with other drugs, particularly those affecting bone marrow function, leading to increased toxicity. Warnings include monitoring for interactions and adjusting dosages accordingly. Always inform your healthcare provider about all medications, supplements, and over-the-counter drugs you are taking before starting Cyclophosphamide.

What should patients know before taking Cyclophosphamide?

Monitor blood counts regularly to detect early signs of hematological toxicity. Be vigilant for signs of infection, such as fever or chills, and seek medical attention immediately. Discuss potential drug interactions with your healthcare provider to minimize risk.

Are Cyclophosphamide side effects well-documented?

Cyclophosphamide has 284,202 adverse event reports on file with the FDA. The drug is frequently reported to cause severe neutropenia and thrombocytopenia, indicating significant risk of life-threatening complications. The volume of reports for Cyclophosphamide reflects both the drug's usage level and the vigilance of the reporting community.

What is the FDA's position on Cyclophosphamide?

The FDA closely monitors cyclophosphamide reports, and regulatory actions may be taken based on emerging safety signals. Patients should report any adverse reactions promptly. For the most current regulatory information, check the FDA's drug labeling database or consult your pharmacist.

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Important Disclaimer: This content is generated by AI analysis of FDA adverse event reports and is provided for informational purposes only. It is not medical advice. Adverse event reports submitted to the FDA do not prove that a medication caused the reported side effect. Always consult your healthcare provider before starting, stopping, or changing any medication. If you experience a serious side effect, contact your doctor or call 911 immediately.